Ionis Pharmaceuticals

IONS

Ionis Pharmaceuticals is a biotechnology company based in Carlsbad, California that specializes in discovering and developing RNA-targeted therapeutics. The company has 3 commercially approved medicines: Spinraza (Nusinersen), Tegsedi (Inotersen), and WAYLIVRA and has 4 drugs in pivotal studies: tominersen for Huntington’s disease, tofersen for SOD1-ALS, AKCEA-APO(a)-LRx for cardiovascular disease, and AKCEA-TTR-LRx for all forms of TTR amyloidosis.The company was named Isis Pharmaceuticals until December 2015.

Ionis Pharmaceuticals has been a target of short sellers for a while. The current short interest of 12.59% is slightly above the average of the last 12 months (9.67%).